Updates

February 22, 2021August 23, 2022
CRISPR Gene Editing Used to Build 1st Model of AML Progression

Blocking early inflammatory and innate immune signaling is a promising therapeutic target in acute myeloid leukemia ... Read more
February 18, 2021February 18, 2021
Potential Therapy May Better Prepare Older Patients Before Stem Cell Transplant

JSP191, an investigational therapy by Jasper Therapeutics, showed promising efficacy as a conditioning agent to prepare ... Read more
February 16, 2021February 17, 2021
Eurordis Survey: Healthcare Experience Worse for Rare Disease Patients

People with rare disorders have a worse healthcare experience than those affected by chronic diseases, according ... Read more
February 15, 2021February 15, 2021
FDA Grants Iadademstat Orphan Drug Designation

The U.S. Food and Drug Administration (FDA) has granted orphan drug designation to Oryzon Genomics‘ iadademstat, ... Read more
February 11, 2021February 11, 2021
Pandemic Won’t Stop Rare Disease Day on Feb. 28

Scores of virtual events are afoot around the world to mark Rare Disease Day 2021 on ... Read more

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